selected publications
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Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing CLN2.
Science translational medicine.
2020
Academic Article
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Times cited: 35 -
Systemic Adeno-Associated Virus-Mediated Gene Therapy Prevents the Multiorgan Disorders Associated with Aldehyde Dehydrogenase 2 Deficiency and Chronic Ethanol Ingestion.
Human gene therapy.
2020
Academic Article
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Times cited: 6 -
Gene Therapy Correction of Aldehyde Dehydrogenase 2 Deficiency.
Molecular therapy. Methods & clinical development.
2019
Academic Article
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Times cited: 22 -
Pathogenic Autoreactive T and B Cells Cross-React with Mimotopes Expressed by a Common Human Gut Commensal to Trigger Autoimmunity.
Cell host & microbe.
2019
Academic Article
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Times cited: 107 -
Gene therapy for C1 esterase inhibitor deficiency in a Murine Model of Hereditary angioedema.
Allergy.
2019
Academic Article
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Times cited: 34 -
Corneal confocal microscopy: Neurologic disease biomarker in Friedreich ataxia.
Annals of neurology.
2018
Academic Article
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Times cited: 24 -
Disease characteristics and progression in patients with late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease: an observational cohort study.
The Lancet. Child & adolescent health.
2018
Academic Article
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Times cited: 87 -
In Vivo Potency Assay for Adeno-Associated Virus-Based Gene Therapy Vectors Using AAVrh.10 as an Example.
Human gene therapy methods.
2018
Academic Article
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Times cited: 8 -
Anti-hIgE gene therapy of peanut-induced anaphylaxis in a humanized murine model of peanut allergy.
The Journal of allergy and clinical immunology.
2016
Academic Article
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Times cited: 18 -
Peri-operative considerations in the patient with primary immune deficiency: a review.
Surgical infections.
2014
Information Resource
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Times cited: 2 -
Disrupted adenovirus-based vaccines against small addictive molecules circumvent anti-adenovirus immunity.
Human gene therapy.
2012
Academic Article
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Times cited: 21 -
AAV-directed persistent expression of a gene encoding anti-nicotine antibody for smoking cessation.
Science translational medicine.
2012
Academic Article
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Times cited: 47 -
AAVrh.10-mediated expression of an anti-cocaine antibody mediates persistent passive immunization that suppresses cocaine-induced behavior.
Human gene therapy.
2012
Academic Article
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Times cited: 38 -
Prevalence of diverticulosis in recurrent Clostridium difficile infection.
World journal of gastroenterology.
2010
Academic Article
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Times cited: 4 -
Thyroid abnormalities in pediatric patients with vitiligo in New York City.
Cutis.
2008
Academic Article
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Times cited: 29 -
Do medical inpatients who report poor service quality experience more adverse events and medical errors?.
Medical care.
2008
Academic Article
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Times cited: 47 -
What can hospitalized patients tell us about adverse events? Learning from patient-reported incidents.
Journal of general internal medicine.
2005
Academic Article
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Times cited: 253