Clinical trial designs for rare diseases: Studies developed and discussed by the International Rare Cancers Initiative Review uri icon

Overview

MeSH Major

  • Neoplasms
  • Randomized Controlled Trials as Topic
  • Rare Diseases

abstract

  • Trials can be designed using a wide array of possibilities. There is no 'one size fits all' solution. In order to make progress in the rare diseases, decisions to change practice will have to be based on less direct evidence from clinical trials than in more common diseases.

authors

publication date

  • January 2015

Research

keywords

  • Review

Identity

Language

  • eng

PubMed Central ID

  • PMC4639696

Digital Object Identifier (DOI)

  • 10.1016/j.ejca.2014.10.027

PubMed ID

  • 25542058

Additional Document Info

start page

  • 271

end page

  • 81

volume

  • 51

number

  • 3