Gene therapy for late infantile neuronal ceroid lipofuscinosis: Neurosurgical considerations Academic Article uri icon

Overview

MeSH Major

  • Aminopeptidases
  • Brain
  • Dependovirus
  • Dipeptidyl-Peptidases and Tripeptidyl-Peptidases
  • Gene Transfer Techniques
  • Genetic Therapy
  • Neuronal Ceroid-Lipofuscinoses
  • Serine Proteases

abstract

  • The neurosurgical considerations and results of this study are presented to offer guidance and a basis for the design of future gene therapy or other clinical trials in children that utilize direct therapeutic delivery.

publication date

  • August 2010

Research

keywords

  • Academic Article

Identity

Language

  • eng

PubMed Central ID

  • PMC3763702

Digital Object Identifier (DOI)

  • 10.3171/2010.4.PEDS09507

PubMed ID

  • 20672930

Additional Document Info

start page

  • 115

end page

  • 22

volume

  • 6

number

  • 2