A randomized study of alglucosidase alfa in late-onset Pompe's disease Academic Article uri icon

Overview

MeSH Major

  • Glycogen Storage Disease Type II
  • alpha-Glucosidases

abstract

  • In this study population, treatment with alglucosidase alfa was associated with improved walking distance and stabilization of pulmonary function over an 18-month period. (ClinicalTrials.gov number, NCT00158600.)

publication date

  • April 15, 2010

Research

keywords

  • Academic Article

Identity

Language

  • eng

Digital Object Identifier (DOI)

  • 10.1056/NEJMoa0909859

PubMed ID

  • 20393176

Additional Document Info

start page

  • 1396

end page

  • 406

volume

  • 362

number

  • 15