Selected publications
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Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study.
Haematologica.
2019
Information Resource
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Times cited: 3 -
Clinical spectrum of pyruvate kinase deficiency: Data from the pyruvate kinase deficiency natural history study.
Blood.
2018
Academic Article
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Times cited: 17 -
Mortality after pediatric arterial ischemic stroke.
Pediatrics.
2018
Academic Article
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Times cited: 5 -
Eltrombopag for children with chronic immune thrombocytopenia (PETIT2): A randomised, multicentre, placebo-controlled trial.
The Lancet.
2015
Academic Article
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Times cited: 88