Selected publications
- Safety and Efficacy of Mitapivat in Pyruvate Kinase Deficiency. New England Journal of Medicine. 2019 Academic Article GET IT
-
Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study.
Haematologica.
2019
Information Resource
GET IT
Times cited: 3 -
Clinical spectrum of pyruvate kinase deficiency: Data from the pyruvate kinase deficiency natural history study.
Blood.
2018
Academic Article
GET IT
Times cited: 17