Selected publications
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The european hematology association roadmap for european hematology research: A consensus document.
Haematologica.
2016
Academic Article
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Times cited: 20 -
Lack of hepcidin ameliorates anemia and improves growth in an adenine-induced mouse model of chronic kidney disease.
American Journal of Physiology - Renal Physiology.
2016
Academic Article
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Times cited: 8 -
Iron and reactive oxygen species: Friends or foes of cancer cells?.
Antioxidants and Redox Signaling.
2014
Review
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Times cited: 27 -
Macrophages support pathological erythropoiesis in polycythemia vera and β-thalassemia.
Nature Medicine.
2013
Academic Article
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Times cited: 105 -
In vivo gene transfer strategies to achieve partial correction of von willebrand disease.
Human Gene Therapy.
2012
Academic Article
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Times cited: 6 -
Therapeutic hemoglobin levels after gene transfer in β-thalassemia mice and in hematopoietic cells of β-thalassemia and sickle cells disease patients.
PLoS ONE.
2012
Academic Article
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Times cited: 37 -
Enhanced erythropoiesis in Hfe-KO mice indicates a role for Hfe in the modulation of erythroid iron homeostasis.
Blood.
2011
Academic Article
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Times cited: 32 -
Hepcidin as a therapeutic tool to limit iron overload and improve anemia in β-thalassemic mice.
Journal of Clinical Investigation.
2010
Academic Article
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Times cited: 125 -
A preclinical approach for gene therapy of β-thalassemia.
Annals of the New York Academy of Sciences.
2010
Academic Article
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Times cited: 12 -
Hepcidin and Hfe in iron overload in β-thalassemia.
Annals of the New York Academy of Sciences.
2010
Review
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Times cited: 12 -
Changes in bone microarchitecture and biomechanical properties in the th3 thalassemia mouse are associated with decreased bone turnover and occur during the period of bone accrual.
Calcified Tissue International.
2010
Academic Article
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Times cited: 10 -
Id1 represses osteoclast-dependent transcription and affects bone formation and hematopoiesis.
PLoS ONE.
2009
Academic Article
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Times cited: 20 -
Decreased differentiation of erythroid cells exacerbates ineffective erythropoiesis in β-thalassemia.
Blood.
2008
Academic Article
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Times cited: 86 -
Protective role of calreticulin in HFE hemochromatosis.
Free Radical Biology and Medicine.
2008
Academic Article
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Times cited: 16 -
Ineffective erythropoiesis in β-thalassemia is characterized by increased iron absorption mediated by down-regulation of hepcidin and up-regulation of ferroportin.
Blood.
2007
Academic Article
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Times cited: 182 -
Therapeutic options for patients with severe β-thalassemia: The need for globin gene therapy.
Human Gene Therapy.
2007
Review
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Times cited: 36 -
Exploring the role of hepcidin, an antimicrobial and iron regulatory peptide, in increased iron absorption in β-thalassemia.
Annals of the New York Academy of Sciences.
2005
Academic Article
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Times cited: 15 -
Progress toward the genetic treatment of the β-thalassemias.
Annals of the New York Academy of Sciences.
2005
Review
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Times cited: 32 -
Globin gene transfer for treatment of the β-thalassemias and sickle cell disease.
Best Practice and Research: Clinical Haematology.
2004
Review
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Times cited: 18 -
Globin gene transfer: A paradigm for transgene regulation and vector safety.
Gene Therapy and Regulation.
2004
Report
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Times cited: 9 -
A novel murine model of Cooley anemia and its rescue by lentiviral-mediated human β-globin gene transfer.
Blood.
2003
Academic Article
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Times cited: 165 -
Therapeutic globin gene delivery using lentiviral vectors.
Current Opinion in Molecular Therapeutics.
2002
Review
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Times cited: 20 -
Successful treatment of murine β-thalassemia intermedia by transfer of the human β-globin gene.
Blood.
2002
Academic Article
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Times cited: 131 -
Therapeutic haemoglobin synthesis in β-thalassaemic mice expressing lentivirus-encoded human β-globin.
Nature.
2000
Academic Article
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Times cited: 410 -
The cHS4 insulator increases the probability of retroviral expression at random chromosomal integration sites.
Journal of Virology.
2000
Academic Article
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Times cited: 160 -
Basic principles of gene transfer in hematopoietic stem cells.
Progress in Experimental Tumor Research.
1999
Review
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Times cited: 4 -
Genetic treatment of severe hemoglobinopathies: The combat against transgene variegation and transgene silencing.
Seminars in Hematology.
1998
Review
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Times cited: 97